Dopa-responsive hypersomnia and mixed movement disorder due to sepiapterin reductase deficiency.

نویسندگان

  • Jennifer Friedman
  • Keith Hyland
  • Nenad Blau
  • Mia MacCollin
چکیده

Sepiapterin reductase deficiency (SRD) is a rare, treatable disorder of monoamine metabolism with cognitive delay and l-dopa responsive movement disorder. We describe a patient with SRD and distinctive phenotypic feature of marked hypersomnolence. Our patient showed improvement with therapies directed at both serotonergic and dopaminergic deficiencies. This case illustrates symptoms that characterize the SRD phenotype and demonstrates the importance of systematic treatment trials addressing the various biochemical abnormalities present.

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عنوان ژورنال:
  • Neurology

دوره 67 11  شماره 

صفحات  -

تاریخ انتشار 2006